GENE THERAPY DISGRACE THE NEXT BIG THING WIRED SKIP START ARTICLE OPEN GO TO HOME PAGE OPEN SEARCH SEARCH BUSINESS CULTURE DESIGN GEAR SCIENCE SECURITY TRANSPORTATION PHOTO VIDEO VIDEO MAGAZINE INSIDER FUTURE MOBILITY FALLBACK IMAGE MONTHS PLUS FREE PORTABLE PHONE YOUR THANK YOU INVALID EMAIL FOLLOW USON TWITTER THE WRONG WAY YOURE DATA FOLLOW FOLLOW FACEBOOK MISS FEATURES YOUTUBE CARL ZIMMER DATE COURTESY UNIVERSITY OF PENNSYLVANIA LABORATORY STRUCTURAL BIOLOGY LIFES WORK CRUMBLE JAMES WILSONS GLIMMER OFFICE THE UNIVERSITY OF PENNSYLVANIA ROLE FOUNDER DIRECTOR INSTITUTE FOR HUMAN WILSON RESEARCHERS GENES PATIENTS REPAIR FAULTY COLLEAGUES ADDING THE ULTIMATE GOAL WAS TO RARE ORNITHINE TRANSCARBAMYLASE GENETIC DISORDER RENDERS VICTIMS PROCESS NITROGEN PROTEIN BROKEN THE BLOOD SUFFERERS POISONED BITE HOT DOG JUST HALF CHILDREN BABIES THE AGE DISEASE GENE ENGINEERED VIRUS CARRYING FUNCTIONAL TRIALS THE VIRUS LAUNCHED CLINICAL TRIAL SAFETY HUMANS SUFFERING TUESDAY MORNING CALL JESSE GELSINGER DOSE TEMPERATURE QUICKLY THE 17 PREVIOUS EXPERIENCED FLULIKE SYMPTOMS THE FOLLOWING MORNING BLOOD TESTS HIGH COAGULATION AS IF YOUNG MANS BODY SEIZED TONE THINGS THE NEXT 48 HOURS THE TEENAGERS CONDITION SKIN EYES TURNED JAUNDICED SIGN LIVER INTENSIVE CARE UNIT INFLAMMATION BLOATED FINANCIAL CONFLICT COMPANY FUNDING ACQUIRED EXCLUSIVE RIGHTS LICENSE RESEARCHER CONTACT LEFT INCREASINGLY DIRE UPDATES LISTENING SCIENTIFIC TRIUMPH DAYS REGULAR COLLEAGUE STEVEN PRINCIPAL INVESTIGATOR PULLED ASIDE CONFIRMED THE STUDY HELP SAVE KIDS LIFE SUPPORT HOPE STUNNED SCIENTISTS DEATH ENTIRE MIGHT EVENTUALLY LIVES THOUSANDS HOSPITAL FAMILY RECOGNIZE JAUNDICE GAVE ASSENT SPECIALIST SHUT OFF THE MACHINES THE ONLY THING THE TEENAGER CAREER FELL JEFF SHOCKED GUANGPING MICROBIOLOGIST TIME WAS ASSOCIATE DIRECTOR OF THE TEAM WORK TO DO HAD TO BEYOND THE EMOTIONS FOCUS EVERYTHING FIGURE THE MONTHS TEAM INVESTIGATE THEMSELVES PENN PORING THE TRIAL LOOKING FDA THE NATIONAL INSTITUTES OF HEALTH SUMMONED SENATE SUBCOMMITTEE DISCUSS RISKS BENEFITS THE WAKE MEDIA COVERAGE THE PUBLIC IMAGE SINISTER ENRAGED LEARNED DETAILS DISCLOSED FACT EQUITY THE ANIMALS SUFFERED SIDE EFFECTS DIDNT THINK THE ANIMAL DEATHS RELEVANT HUMAN TRIALS HIGHER VIRUSES STATE OF AFFAIRS DONNA SHALALA SECRETARY OF THE DEPARTMENT OF HEALTH AND HUMAN SERVICES THE NEW ENGLAND JOURNAL OF SOON MIRED SUED LEAD THE UNIVERSITY THE CASE SETTLED THE JUSTICE DEPARTMENT CASE SETTLE CONSEQUENCE THIS ONE FIELD PUNISHMENT HANDED BANNED HUMAN CLINICAL TRIALS DOWN POSITION HELM THE INSTITUTE FOR HUMAN GENE THERAPY PROFESSOR AFTERWARD THE INSTITUTE ITSELF COMPOUNDING PALL DOTCOM CRASH WIPED MONEY PROMISED FUEL IN SEPTEMBER CUSP BREAKTHROUGH THE END CAUTIONARY TALE PEOPLE GIVEN UP INVESTORS RUNNING COULDNT LET GO CHOSE NEW WAY HELPED BACK FROM THE DEAD PATH YOUNG SCIENTIST TRACKED THE ASCENT SIMULTANEOUSLY MEDICAL DEGREE THE UNIVERSITY OF MICHIGAN STUDY DISORDER CAUSES HOST TERRIBLE SYMPTOMS RANGING ARTHRITIS PARTICULAR DEFECT NO IDEA HOW TO TRANSLATE DISCOVERY THE JOURNAL SUDDENLY UNDERSTOOD DOCTORS SOMEDAY CURE GENETIC DISORDERS ONCE INCURABLE STANFORD BIOLOGISTS RICHARD MULLIGAN PAUL FIGURED TRANSPLANT EFFECTIVELY REWRITING PHRASE FLOATING MEDICAL CIRCLES ITS TIME WIFE BOSTON LEARN TRANSPLANTATION NEARLY MULLIGANS TUTELAGE MICHIGAN FIRST DISEASE FAMILIAL HYPERCHOLESTEROLEMIA THE PATIENT LACKS RECEPTORS BAD CHOLESTEROL NORMALLY HAVE HEART SOMETIMES VECTOR ATTACK VERSION LOADED TESTED TYPE RABBIT GENETICALLY PRONE LOWERED HUMAN TRIAL WOMAN SURGEONS INFECTED CELLS HOLD PUBLISHED MILESTONE EXPERIMENT REVERSE INHERITED THE NEW YORK TIMES PAPER REPORT THERAPEUTIC THANKS TO THE GREEN LIGHT CLINICAL TRIALS JUMPING FROM ZERO IN 1999 UNIVERSITIES STAKE A CLAIM NEW FIELD STAFF SEQUEL WANTED THE SURGERY THE SCIENTIFIC LITERATURE SEEK ADENOVIRUSES CAUSING THE COMMON COLD GOOD MOVING FORWARD CHILDRENS HOSPITAL OF TIMES CONFERENCE ROOM LAB FRAMELESS SPECTACLES GIVE FACE MONASTIC WARDROBE SUGGESTS TRIP THE COUNTRY CLUB KHAKI PANTS BLUE WHOSE LOGO HORSES ANSWERS QUESTION THINKS PEAKING NUMBER ONGOING THE US WE USED TO LONGER LECTURES JOIN ONTO HIMSELF SMALLER ENERGY HAD GONE WRONG CLEAR REACHED TEENS IMMUNE SYSTEM UNLEASHED WILD EXPOSED PREVIOUSLY ADENOVIRUS WHEN HE CAME ANTIBODIES TRIGGERED SUDDEN EXPLOSION ADVICE TACHI YAMADA MEDICAL SCHOOL CHAIR SMITHKLINE BEECHAM STINT AT THE GATES YAMADA TAKEDA PHARMACEUTICALS DEALING CRISIS TRYING GROUP GOING TO GIVING UP PUSHED SOLVE PROBLEM PROSPECTS TURNING THE LIGHT TACHI SURE DO IT RIGHT SOMETHING MORE GRANT FUND FIND DNA TRIGGERING POTENTIALLY IMMUNE HABIT SHOWING UP CULTURES SICK JUDE THE UNIVERSITY OF NORTH CAROLINA THE IMMUNE SYSTEM BARELY NOTICE THE HEIGHT INSPIRED KIND BETTER THAN AAV2 MUSCLE CELLS LESS EFFECTIVE RESEARCH MINIMAL RESPONSE PARAMOUNT ONES DEVELOPED TECHNIQUE DISCOVERING SCORES TISSUE NONE STRONG IMMUNE REACTION HUNDRED EFFICIENT GEMS THE BRAIN BLOODSTREAM SOMETHING ALMOST DONE KEPT GIFT THE FIELD BLOW LAID WASTE DISCOVERED AAVS PROPERTIES RATHER HOAR